With advances in our understanding of the molecular biology of human diseases and the development of efficient gene transfer techniques, the treatment of such d
This text brings together the current data previously separated. It combines information on gene therapy technologies and the attendant regulatory requirements
Recognizing the potential design complexities and ethical issues associated with clinical trials for gene therapies, the Forum on Regenerative Medicine of the N
Since the discovery of the molecular structure of genes and the unveiling of the molecular basis of numerous human diseases, scientists have been fas- nated wit
The clinical applications of human gene therapy have been particularly fruitful in oncology, and in the past two decades there has been explosive growth in unde